Browsing by Author Manno, CS
Showing results 1 to 3 of 3
Preview | Issue Date | Title | Author(s) | Advisor | Type |
| 2006 | Successful transduction of liver in hemophilia by AAV-factor IX and limitations imposed by the host immune response | Manno, CS; Arruda, VR; Pierce, GF; Glader, B; Ragni, M; Rasko, J; Ozelo, MC; Hoots, K; Blatt, P; Konkle, B; Dake, M; Kaye, R; Razavi, M; Zajko, A; Zehnder, J; Nakai, H; Chew, A; Leonard, D; Wright, JF; Lessard, RR; Sommer, JM; Tigges, M; Sabatino, D; Luk, A; Jiang, HY; Mingozzi, F; Couto, L; Ertl, HC; High, KA; Kay, MA | - | Artigo de periódico |
| 2003 | AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B | Manno, CS; Chew, AJ; Hutchison, S; Larson, PJ; Herzog, RW; Arruda, VP; Tai, SJ; Ragni, MV; Thompson, A; Ozelo, M; Couto, LB; Leonard, DGB; Johnson, FA; McClelland, A; Scallan, C; Skarsgard, E; Flake, AW; Kay, MA; High, KA; Glader, B | - | Artigo de periódico |
| 2006 | Evidence of multiyear factor IX expression by AAV-mediated gene transfer to skeletal muscle in an individual with severe hemophilia B | Jiang, HY; Pierce, GF; Ozelo, MC; de Paula, EV; Vargas, JA; Smith, P; Summer, J; Luk, A; Manno, CS; High, KA; Arruda, VR | - | Artigo de periódico |